Search for Clinical Trial Results
Mucopolysaccharidosis Type IIIA - 19 Studies Found
Status | Study |
Completed |
Study Name: Intracerebral Gene Therapy for Sanfilippo Type A Syndrome Condition:
Date: 2011-11-10 Interventions: Genetic: SAF-301 The treatment plan consists on a direct injection of the investigational medicinal prod |
Enrolling by invitation |
Study Name: An Extension Study to Determine Safety and Efficacy for Pediatric Patients With MPS Type IIIA Disease Who Participated in Study HGT-SAN-093. Condition:
Date: 2015-01-21 Interventions: Drug: HGT-1410 HGT-1410 administered according to Patient Group assignment. |
Recruiting |
Study Name: A Study of Mucopolysaccharidosis Type IIIB (MPS IIIB) Condition:
|
Recruiting |
Study Name: Lysosomal Storage Disease: Health, Development, and Functional Outcome Surveillance in Preschool Children Condition:
|
Terminated |
Study Name: ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases Condition:
|
Completed |
Study Name: HSCT for High Risk Inherited Inborn Errors Condition:
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RECRUITING |
Study Name: Study of DNL126 in Pediatric Participants With Mucopolysaccharidosis Type IIIA (Sanfilippo Syndrome Type A) Condition: Mucopolysaccharidosis Type IIIA Date: 2024-05-11 Interventions: intravenous repeating dose |